AUTHOREA
Log in Sign Up Browse Preprints
LOG IN SIGN UP
Izabela Kranjčec
Izabela Kranjčec

Public Documents 1
Genetic testing facilitates correct diagnosis and directs management of unexplained p...
Izabela Kranjčec
NUŠA MATIJAŠIĆ STJEPOVIĆ

Izabela Kranjčec

and 6 more

August 24, 2024
Despite thorough medical assessment, diagnosis of inherited bone marrow failure syndrome (IBMFS) is often significantly delayed. Genomic investigations have been more often used to facilitate correct diagnosis and guide management in unexplained childhood cytopenias. We present two cases of unrelated adolescent girls with bicytopenia, unremarkable medical history and normal physical features who were diagnosed with nonclassical IBMFS ( ERCC6L2) using genetic evaluation. ERCC6L2-associated disease has been so far frequently related to neurodevelopmental delay and consanguinity and recognized as a predisposition syndrome to myeloid malignancies. Genetic testing should, therefore, be included in the contemporary approach to chronic cytopenias in children.

| Powered by Authorea.com

  • Home